A Multicenter Multinational Observational Study of Children With Hypochondroplasia
← catalyst calendarNCT06212947 · readout in 6,343 d
Sponsored by BioMarin Pharmaceutical (industry) · BMRN — their whole pipeline →.
Phase
—
Status
Recruiting
Study type
Observational
Enrollment
400estimated
Sites
43
Countries
Argentina, Australia, Brazil +8
Every value on this page is a field the sponsor filed with ClinicalTrials.gov, reproduced. Dates are their own estimates, revised as a study runs, unless the registry marks them actual. sources →
Source: ClinicalTrials.gov, retrieved 2026-08-19
Dates
each axis at the precision it was filed, with the registry's own basis| Date | Filed | Basis | What it is |
|---|---|---|---|
| Start | 2023-11-27 | actual | When the study began enrolling |
| Primary completion | 2043-12-31 | estimated | The date the last participant is measured for the primary outcome — the readout window |
| Study completion | 2043-12-31 | estimated | The whole study's end, after follow-up |
| First posted | 2024-01-19 | actual | When this record first appeared on the registry |
| Results posted | — | When the sponsor posted results to the registry | |
| Record updated | 2025-04-03 | actual | The sponsor's own last edit to this record — every projection above is as current as this date |
What it studies
Condition
- Hypochondroplasia
Primary outcomes
what the primary-completion date above is the date OFChange in annualized growth velocity (AGV)
measured Every 6 months through end of study, up to 15 years
Change in Height Z-score
measured Every 6 months through end of study, up to 15 years
Change in Height
measured Every 6 months through end of study, up to 15 years
Change in BMI
measured Every 6 months through end of study, up to 15 years
Change in BMI Z-score
measured Every 6 months through end of study, up to 15 years
Change in ratios of upper to lower body segments
measured Every 6 months through end of study, up to 15 years
Change in ratios of upper and lower leg length ratio
measured Every 6 months through end of study, up to 15 years
Change in ratio of arms span to standing height ratio
measured Every 6 months through end of study, up to 15 years
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